Research Focus

The Gene Transfer Laboratory is dedicated to investigating the role of localized mitochondrial DNA variations in the development and progression of neurodegenerative diseases, particularly focusing on Leber hereditary optic neuropathy (LHON), Maternally Inherited Leigh Syndrome (MILS), and Neurogenic Ataxia and Retinitis Pigmentosa (NARP). Utilizing cutting-edge mito-targeting technologies, our goal is to uncover novel therapeutic approaches for the treatment of LHON and other mitochondrial genetic diseases.